Researchers have shown that gene therapy can help people with β-thalassemia, an inherited blood disorder that cripples the oxygen-carrying protein called hemoglobin, BBC reports. An international team delivered a corrective gene into blood stem cells taken from patients, then reinfused the cells into the body. Fifteen of 22 patients no longer require blood transfusions and others need them less often, the scientists reported yesterday in The New England Journal of Medicine.
Emmanuel Ifeanyi Obeagu
Hi, it is a great feat in Transfusion medicine. I believe gene therapy will handle many haemoglobinopathies in World.
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Hatem Zayed
Great steps, however the hurdle of the field now is to sustain long-term expression without insertional mutagenesis and/or oncogene activation.
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